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L’acétyl(cyanoacétyl)carbamate est utilisé dans la synthèse d’inhibiteurs ciblant le domaine PDZ de PICK1, qui est une cible potentielle pour l’ischémie cérébrale, la douleur et les maladies de dépendance. Il est également utilisé dans la synthèse d’inhibiteurs de la cathéspine K.